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Leucèmia i hemopaties pediàtriques

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Publicacions

  • Río P, Zubicaray J, Navarro S, Gálvez E, Sánchez-Domínguez R, Nicoletti E, Sebastián E, Rothe M, Pujol R, Bogliolo M, John-Neek P, Bastone AL, Schambach A, Wang W, Schmidt M, Larcher L, Segovia JC, Yáñez RM, Alberquilla O, Díez B, Fernández-García M, García-García L, Ramírez M, Galy A, Lefrere F, Cavazzana M, Leblanc T, García de Andoin N, López-Almaraz R, Català-Temprano A, Barquinero J, Rodríguez-Perales S, Rao G, Surrallés J, Soulier J, Díaz-de-Heredia C, Schwartz JD, Sevilla J and Bueren JA.

    Haematopoietic gene therapy of non-conditioned patients with Fanconi anaemia-A: results from open-label phase 1/2 (FANCOLEN-1) and long-term clinical trials.

    Lancet . 404(10471): 2584-2592. Nº de cites: 15

    [doi:10.1016/S0140-6736(24)01880-4]

  • Rey-Barroso L, Roldan-Molina M, Frías M, Burgos-Fernández FJ, Isola I, Ruiz-Llobet A, Sarrate E and Vilaseca M.

    Optimized protocol for intracellular labeling of red blood cells with anti-hemoglobin F for confocal microscopy analysis

    MICRON . 199: 103913-103913.

    [doi:10.1016/j.micron.2025.103913]

  • Illarregi U, Bilbao-Aldaiturriaga N, Gutierrez-Camino A, Martinez de Estibariz I, Arzuaga-Mendez J, Camós-Guijosa M, Ramirez-Orellana M, Astigarraga I, Richer C, Sinnett D, Martin-Guerrero I and Lopez-Lopez E.

    surviBALL: exploring lncRNA expression at diagnosis for 5-year EFS risk stratification in pediatric B-ALL-a proof of concept.

    Molecular and Cellular Pediatrics . 12(1): 19-19.

    [doi:10.1186/s40348-025-00210-3]

  • Cesaro, S, Verheggen, I, Tridello, G, Styczynski, J, Roeven, WHM, Hwang, A, Stamouli, M, Petrov, Y, Ben Abdeljelil, N, Mazilier, P, Zaidman, I, Tambaro, FP, Elias, S, Verna, M, Marsal-Ricoma J, Karas, M, Corral, LL, Goussetis, E, Cerretti, R, Perruccio, K, Hornakova, M, Wölfl, M, Nordlander, A, Biffi, A, Spadea, M, Salinas, AS, Bramanti, S, Belendez, C, Skert, C, Gozdzik, J, Cuoghi, A, Mas, MH, Pennisi, M, de Becker, A, Richardson, D, Peric, Z, de la Camara, R and Averbuch, D.

    A survey on the practices and the management of hemorrhagic cystitis in patients who undergo allogeneic hematopoietic stem cell transplantation, on behalf of the Infectious Diseases Working Party of EBMT.

    BONE MARROW TRANSPLANTATION . 60(11): 1480-1486.

    [doi:10.1038/s41409-025-02703-1]

  • Ghanjati, F, Heck, A, Lebrecht, D, Nöllke, P, Andresen, F, Rotari, N, Schoof, M, Schönung, M, Lipka, DB, Dworzak, M, De Moerloose, B, Sukova, M, Hasle, H, Jahnukainen, K, Malone, A, Masetti, R, Buechner, J, Ussowicz, M, Català-Temprano A, Turkiewicz, D, de Haas, V, Schmugge, M, Erlacher, M, Niemeyer, CM and Flotho, C.

    Epigenetic risk stratification in juvenile myelomonocytic leukemia by targeted methylation analysis of the BMP4 locus

    CLINICAL EPIGENETICS . 17(1): .

    [doi:10.1186/s13148-025-01983-0]

  • Fuentes P, García-Peydró M, Alcain J, Mosquera M, Cela C, Cifuentes C, Torrebadell-Burriel M, Isola I, Camós-Guijosa M, Ramírez M, Alarcón B and Toribio ML.

    Pre-TCR-targeted immunotherapy for T cell acute lymphoblastic leukemia

    NATURE IMMUNOLOGY . 26(10): 1712-1725. Nº de cites: 3

    [doi:10.1038/s41590-025-02265-w]

  • Iriondo J, Zubicaray J, Río P, Català-Temprano A, Solsona M, Sanz A, Gómez A, Sebastián E, de la Cruz A, Galán A, Navarro S, Larcher L, de Andoin NG, Uriz JJ, Vagace JM, Gonzalez de Pablo J, Pujol MR, Nicoletti E, Surrallés J, Martín-Prado S, Schwartz JD, Soulier J, Bueren JA and Sevilla J.

    Eltrombopag for Bone Marrow Failure in Fanconi Anemia: Results From the Phase II Clinical Trial FANCREV

    EUROPEAN JOURNAL OF HAEMATOLOGY . 115(4): 403-412.

    [doi:10.1111/ejh.70007]

  • Bartoló-Ibars A, Aran A, Johansson AM, Ortiz-Maldonado V, Klein-González N, Alonso-Saladrigues A, James E, Urbano-Ispizua A, Rives-Solà S, Delgado J, González-Navarro EA, Kwok WW and Juan-Otero M.

    T-cell responses against CD19-targeted CAR T cells varnimcabtagene autoleucel (ARI-0001): implications for immune response and therapy outcomes

    Journal for ImmunoTherapy of Cancer . 13(9): .

    [doi:10.1136/jitc-2024-010792]

  • Romero-Moya D, Torralba-Sales E, Calvo C, Marin-Bejar O, Magallon-Mosella M, Distefano-Muñoz ME, Pera J, Juan Castaños Asins, De Giorgio F, Gonzalez J, Iglesias A, Berenguer-Balaguer C, Schilling M, Plass M, Pasquali L, Català-Temprano A, Molina O, Wlodarski MW, Bigas A and Giorgetti A.

    CRISPR-engineered human GATA2 deficiency model uncovers mitotic dysfunction and premature aging in HSPCs, impairing hematopoietic fitness

    Leukemia . : .

    [doi:10.1038/s41375-025-02771-8]

  • Awasthi R, Grupp SA, Waldron E, Yanik GA, Tam CS, Rives-Solà S, McGuirk JP, Pulsipher MA, Jaeger U, Myers GD, Borchmann P, Schuster SJ, Stefanski HE, Bishop MR, Chakraborty A, Masood A, Baruchel A and Waller EK.

    Evaluation of in vivo CAR transgene levels in tisagenlecleucel-treated patients with relapsed/refractory B-ALL and DLBCL

    blood advances . 9(17): 4405-4414.

    [doi:10.1182/bloodadvances.2024014995]