Publicacions
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Río P, Zubicaray J, Navarro S, Gálvez E, Sánchez-Domínguez R, Nicoletti E, Sebastián E, Rothe M, Pujol R, Bogliolo M, John-Neek P, Bastone AL, Schambach A, Wang W, Schmidt M, Larcher L, Segovia JC, Yáñez RM, Alberquilla O, Díez B, Fernández-García M, García-García L, Ramírez M, Galy A, Lefrere F, Cavazzana M, Leblanc T, García de Andoin N, López-Almaraz R, Català-Temprano A, Barquinero J, Rodríguez-Perales S, Rao G, Surrallés J, Soulier J, Díaz-de-Heredia C, Schwartz JD, Sevilla J and Bueren JA.
Haematopoietic gene therapy of non-conditioned patients with Fanconi anaemia-A: results from open-label phase 1/2 (FANCOLEN-1) and long-term clinical trials.
Lancet . 404(10471): 2584-2592. Nº de cites: 6
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Silbert SK, Rankin AW, Hoang CN, Semchenkova A, Myers RM, Zerkalenkova E PhD, Wang HW, Kovach AE, Yuan CM, Delgado Colon D, Vasseur L, Bataller A, John S, Utley Lyons K, Friedes BD, Alonso-Saladrigues A, Abdel-Azim H, Balducci E, Aljudi A, Balsat M, Biery DN, Chamdin A, Chang BH, Cuevo RS MD, De Moerloose B, Dickens DS, Duffner UA, Duployez N, El Chaer F, Elliott MA, Escherich G, Fernandes S, Fitzjohn MR, Gahvari ZJ, Grupp SA, He RR MD, Harrison C, Hergott CB, Hsieh EM, Kim AS, Kuo DJ, Larson DP, Lee BJ, Leguay TT, Lindsley RC, Mangaonkar AA, Mezger K, Pacenta HL, Pan J, Provost MRM, Puri L, Raikar SS, Martinez AJ, Bristol IQ, Murphy KD, Reiman L, Redell MS, Reed K, Roth Guepin G, Rubinstein JD, Savasan S, Schafernak KT, McLean Stevens A, Talleur AC, Torres Carapia N, Vargaftig J, Vatsayan A, Wölfl M, Zhao L, Rives-Solà S, Fabrizio VA, Sasaki K, Aldoss I, Boissel N, Rheingold SR, Davis KL, Ghorashian S, Jacoby E, Popov A, Lamble AJ and Shah NN.
Project EVOLVE: an international analysis of postimmunotherapy lineage switch, an emergent form of relapse in leukemia.
Blood . 146(4): 437-455.
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Kotmayer L, Kozyra EJ, Kang G, Strahm B, Yoshimi A, Sahoo SS, Pastor VB, Attardi E, Voss R, Vinci L, Kaiser M, Dworzak MN, De Moerloose B, Sukova M, Starý J, Hasle H, Jahnukainen K, Polychronopoulou S, Kállay K, Smith OP, Malone A, Barzilai Birenboim S, Masetti R, Buechner J, Ussowicz M, Kjöllerström P, Bodova I, Kavcic M, Català-Temprano A, Turkiewicz D, Schmugge M, de Haas V, Okhomina VI, Sotomayor C, Catalán P, Wehr C, Salzer U, Germing U, Gattermann N, Bödör C, Gray N, Lewis S, Shimamura A, Giorgetti A, Erlacher M, Niemeyer CM and Wlodarski MW.
Age-dependent phenotypic and molecular evolution of pediatric MDS arising from GATA2 deficiency.
BLOOD CANCER JOURNAL . 15(1): 121-121.
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CastilloSD, Perosanz X, Ressler AK, Ivars M, Rodriguez J, Rovira-Zurriaga C, Nola EM, Llena J, Grego-Bessa J, Roldan-Molina M, Arnau R, Martínez-Romero A, Barber-Martínez de la Torre I, Miguel Bejarano Serrano, Vicente-Villa MA, Celis-Passini V, Salvador-Hernandez H, Mora J, Marchuk DA, Baselga E and Graupera M.
Somatic Uniparental Disomy of PTEN in Endothelial Cells Causes Vascular Malformations in Patients with PTEN Hamartoma Tumor Syndrome
CANCER DISCOVERY . 15(7): 1350-1362. Nº de cites: 2
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Tirado N, Fidyt K, Mansilla MJ, Garcia-Perez A, Martínez-Moreno A, Vinyoles M, Alcain J, García-Peydró M, Roca-Ho H, Fernandez-Fuentes N, Guerrero-Murillo M, Falgàs A, Velasco-Hernandez T, Bueno C, Panelli P, Mulens-Arias V, Apostolov A, Engel P, González EA, Vick B, Jeremias I, Caye-Eude A, Baruchel A, Cavé H, Genescà E, Ribera J, Díaz-Beyá M, Martínez-Sánchez MV, Fuster JL, Escudero López A, Minguillón J, Pérez-Martínez A, Ramírez-Orellana M, Torrebadell-Burriel M, Díaz VM, Toribio ML, Sánchez-Martínez D and Menéndez P.
CAR-T cells targeting CCR9 and CD1a for the treatment of T cell acute lymphoblastic leukemia.
JOURNAL OF HEMATOLOGY & ONCOLOGY . 18(1): 69-69.
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Falgàs A, Lázaro-Gorines R, Zanetti SR, Rubio-Pérez L, Martinez-Moreno A, Vinyoles M, Guerrero-Murillo M, Fernandez-Fuentes N, Roca-Ho H, Tirado N, Panisello C, Velasco-Hernandez T, Mayado A, Pérez-Pons A, Genesca E, Ribera JM, Ribera J, Camós-Guijosa M, Ramírez-Orellana M, Anguita E, Ballerini P, Fuster JL, Juan-Otero M, González-Navarro EAA, Locatelli F, Stam RWW, Querol S, Velasco P, Ortiz-Maldonado V, Martínez-Cibrian N, Delgado J, Orfao A, Alvarez-Vallina L, Bueno C and Menendez P.
A TIM-3-Fc decoy secreted by engineered T cells improves CD19 CAR T-cell therapy in B-cell acute lymphoblastic leukemia.
Blood . 145(22): 2599-2613. Nº de cites: 1
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Berrueco R, Soto I, Bastida JM, Calvo Villas JM, de Cos C, Haya S, García FS and Mateo Arranz J.
Patient-Centred Management of Well-Controlled Haemophilia: Obtaining Opinions and Definitions Through a Delphi Consensus
Journal of Clinical Medicine . 14(10): .
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Vicente-Garces C, Fernandez-Isern G, Esperanza-Cebollada E, Richarte M, Crespo-Carrasco A, Montesdeoca S, Isola I, Sarrate E, Cuatrecasas E, Rives-Solà S, Dapena JL, Camós-Guijosa M and Vega-García N.
RNA-sequencing: A reliable tool to unveil transcriptional landscape of paediatric B-other acute lymphoblastic leukaemia
BRITISH JOURNAL OF HAEMATOLOGY . 206(5): 1355-1365.
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Mato S, Carità L, Colmenero A, Andrés M, Balagué O, Andión M, Astigarraga I, Celis-Passini V, Mendoza C, Guerra-García P, Valero L, Galera A, Tallón M, Pol M, Castrejón-de-Anta N, Frauenfeld L, Garcia N, Campo E, Salaverria I and Verdú-Amorós J.
Comprehensive analysis of relapsed-refractory mature B-cell non-Hodgkin lymphoma in children and adolescents
BRITISH JOURNAL OF HAEMATOLOGY . 206(5): 1390-1396.
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Velasco Puyo P, Christou S, Campisi S, Rodríguez-Sánchez MA, Reidel S, Perez-Hoyo S, Mota M, Savvidou I, Rekleiti A, Salvo A, Voi V, Ferrero GB, Mandrile G, Gaglioti CM, Cela E, Ponce-Salas B, Bardón-Cancho EJ, Flevari P, Voskaridou-Dimoula E, Nur E, Biemond BJ, Delaporta P, Beneitez-Pastor D, Collado Gimbert A, Spasiano A, Besse-Hammer T, Lafiatis IG, Dedeken L, Raso S, Ruiz-Llobet A, Bagnato S, Labarque V, Glenthøj A, Ruffo GB, Guerzoni ME, Hafraoui K, Pistoia L, Rosso R, Tagliaferri L, Gonzalez-Urdiales P, Benghiat FS, de Montalembert M, Teles MJ, Vanderfaeillie A, Bertoni E, Cuzzubbo D, Ferreira T, Saunders CJ, Stiakaki E, Van de Velde AL, Diamantidis MD, Kerkhoffs JH, Oliveira MI, Quota A, Russo R, Van Damme A, Argüello Marina M, Lorite Reggiori M, Rijneveld AW, Rodríguez Gallego A, Colombatti R, Iolascon A, Taher A, Gulbis B, Roy NBA and Mañú-Pereira MDM.
COVID-19 in patients affected by red blood cell disorders, results from the European registry ERN-EuroBloodNet
ORPHANET JOURNAL OF RARE DISEASES . 20(1): 183-183.